BioMarin Pharmaceutical Inc. announced today an update to its previously reported interim results of an open-label Phase 1/2 study of BMN 270, an investigational gene therapy treatment for severe hemophilia A. The updated results will be presented by John Pasi, Ph.D. F.R.C.P, at Barts and the London School of Medicine and Dentistry and Haemophilia Clinical Director at Barts Health NHS Trust and primary investigator for the BMN 270 Phase 1/2 clinical trial, during an oral presentation at the International Society on Thrombosis and Haemostasis (ISTH) 2017 Congress being held July 8-13, 2017 in Berlin, Germany.  Professor Pasi will present the data in a late breaking abstract on July 11, 2017, which will be the only clinical data in gene therapy for hemophilia A to be presented at the meeting.

http://investors.biomarin.com/2017-07-11-BioMarins-Investigational-Gene-Therapy-for-Hemophilia-A-at-6e13-vg-kg-Dose-Maintains-Average-Factor-VIII-Levels-within-Normal-Range-for-over-One-Year

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